CHANGING WHAT’S POSSIBLE
FOR BETA-THALASSEMIA

Beta-thalassemia—a serious blood disorder requiring ongoing care

Beta-thalassemia affects the body’s ability to produce functional hemoglobin and often requires lifelong transfusions.

Beta-thalassemia is a rare, inherited blood disorder that reduces the body’s ability to produce functional hemoglobin. Many patients require ongoing transfusions, creating a significant long-term treatment burden.

Our therapeutic approach is designed to address the underlying genetic cause of the disease, with the goal of reducing or eliminating the need for ongoing transfusions.

Discover our one-time treatment for beta-thalassemia

Explore

Patient Spotlight

Meet Priyanka, living with beta-thalassemia, who continues to build a full life while advocating for greater awareness and support.

 

“I try not to let thalassemia hold me back. I try to have a somewhat normal life.”

Patient Spotlight

Meet Priyanka, living with beta-thalassemia, who continues to build a full life while advocating for greater awareness and support.

 

“I try not to let thalassemia hold me back. I try to have a somewhat normal life.”

Beta-thalassemia Support

Managing beta-thalassemia often involves ongoing care and long-term treatment. The organization in the link below provides helpful resources, support, and connections for individuals and families navigating the condition.

Find Support

Continue Exploring

Treatment Centers

Find a Qualified Treatment Center and take the next steps towards care

Genetix CARES

Explore our white-glove support designed for patients navigating the treatment journey